Research, Education and Family support for WAS families worldwide
Patients & Families
Find a Doctor
Find a Clinical Trial
The research and development for Gene Therapy Trials in France, U.K. and U.S.A. is sponsored by the French Muscular Dystrophy Association (AFM), raising funds for rare diseases through the annual telethon in France. AFM funds the Genethon laboratory which has conducted the pharmaceutical development and sponsors the U.K. and French trials.
Contact Information:
France
Germany
Italy
U.K.
U.S.A.
Back to top > Next Section: Transplant Trials